rarediseases 2022

Clinical Research and Treatment

Rare diseases give the opportunities to study human physiology and biomedical science from interesting perspectives. Major scientific breakthroughs resulting from study of rare diseases. Researchers are increasingly working through networks in order to share the results of their research and to advance more effectively. The satisfaction of diagnosing a patient with a rare disorder successfully is often rapidly countered by the realization that the capacity to understand and treat the patient’s condition is limited by ignorance and the difficulties of studying the disease. An orphan drug is a medicinal product developed for the treatment of rare diseases. For all rare diseases, science can provide some answers.